Research: Correlates of tuberculosis risk: Predictive biomarkers for progression to active tuberculosis

14 Nov 2016
Biomarker TB risk
14 Nov 2016

SATVI authors, Mark Hatherill and Tom Scriba have co-authored "Correlates of tuberculosis risk: Predictive biomarkers for progression to active tuberculosis" appearing in the European Respiratory Journal.

Biomarker TB risk

 

New approaches to control the spread of tuberculosis (TB) are needed, including tools to predict development of active TB from latent TB infection (LTBI). 

Correlate of TB risk
Outcome of M. tuberculosis infection is therefore not a simple two-state distribution represented by either LTBI or active TB, but rather represents a continuous spectrum of states that differ by pathogen and host “activity”, which require different diagnostic and treatment strategies (figures 1 and 2).

Outcome of Mycobacterium tuberculosis transmission and establishment of infection or disease based on the correlates of disease and correlates of risk. The outcome of a primary or secondary M. tuberculosis infection is not a simple two-state distribution represented by either active tuberculosis (TB) or latent TB infection, but rather represents a continuous spectrum of states that differ by the degree of the pathogen replication, host resistance and inflammatory markers. The identification of M. tuberculosis infection is complex, due to the absence of clinical signs, correlates of disease (COD), lung lesions detected by chest radiography or M. tuberculosis in the sputum culture. The latency state is characterised by an immunological equilibrium and by presumed control of the bacterial replication. As the infection advances, this balance is lost, resulting in increased bacterial burden and/or increased pathology. This state can be identified as subclinical or incipient TB disease, in which CODs may still be poorly informative. In contrast, correlates of risk (COR) may potentially allow the identification of those at risk, for preventive treatment. Indeed, upregulation of interleukin (IL)-13 and type I and II interferon (IFN)-related gene expression, elevated activation markers on T-cells (e.g. expression of D-related human leukocyte antigen and loss of CD27 expression), as well as an elevated monocyte/lymphocyte (M/L) ratio, have been shown to be predictive of TB disease development. The progression of subclinical TB to clinical TB is likely to be associated with a further increase in bacterial burden and/or pathology. Therefore, active TB diagnosis is based on CODs, including chest radiography findings such as lung lesions indicative of disease, detection of M. tuberculosis in sputum and positive COR tests. Transmission of M. tuberculosis from active TB patients may lead to a primary or secondary M. tuberculosis infection. Primary M. tuberculosis infection is defined by IFN-γ release assay (IGRA)/tuberculin skin test (TST) conversion and absence of radiological lung lesions and sputum negative for M. tuberculosis. ↓: downregulation; ↑: upregulation; +: presence of a modulation based on current knowledge; −: absence of a modulation based on current knowledge.

Figure 2 Correlate of TB risk
Figure 2: Correlates of tuberculosis (TB) disease, infection and risk of disease. Evaluation of tests to detect active TB disease, subclinical TB disease, incipient TB disease, infection and cleared infection. M. tuberculosisMycobacterium tuberculosis; TST: tuberculin skin test; IGRA: interferon-γ release assay; COR: correlates of risk; M/L: monocyte/lymphocyte.

These efforts have included unbiased approaches employing “omics” technologies, as well as more directed, hypothesis-driven approaches assessing a small set or even individual selected markers as candidate correlates of TB risk. Unbiased high-throughput screening of blood RNAseq profiles identified signatures of active TB risk in individuals with LTBI, ⩾1 year before diagnosis.

A recent infant vaccination study identified enhanced expression of T-cell activation markers as a correlate of risk prior to developing TB; conversely, high levels of Ag85A antibodies and high frequencies of interferon (IFN)-γ specific T-cells were associated with reduced risk of disease. Others have described CD27−IFN-γ+ CD4+ T-cells as possibly predictive markers of TB disease. T-cell responses to TB latency antigens, including heparin-binding haemagglutinin and DosR-regulon-encoded antigens have also been correlated with protection.

Candidates of TB risk

Biomarker Neonates, children, adolescent or adult population Location [Ref.]
Validated correlates of TB risk        
 Commercial or traditional tests  for LTBI diagnosis RD1-specific immune response in IGRA, immune sensitisation to PPD in TST Children and adults Global [22, 44, 45]
 Molecular tests mRNA expression signature of 16 IFN response genes Adolescents Africa [52]
 Cell activation markers Increased HLA-DR-expressing CD4+ T-cells Infants Africa [63]
 Blood cell counts Elevated monocyte/lymphocyte ratio Adults Africa [111, 114]
Unvalidated correlates of TB risk        
 Molecular tests IL-13 and AIRE mRNA expression signature Adults Europe [58–60]
  Elevated expression signatures of IFN response and T-cell genes Infants with strong response to BCG vaccination Africa [115]
Elevated expression signatures of inflammation, myeloid and glucose metabolism genes Infants with weak response to BCG vaccination Africa [115]
 Antigen-specific T-cells Increased IFN-γ-expressing Ag85A-specific T-cells Infants Africa [63]
  Increased Th1-cytokine-expressing BCG-specific CD4+ T-cells Infants with strong response to BCG vaccination Africa [115]
 Cell differentiation markers Downmodulation of CD27 in CD4+ T-cells Adults Africa [76]
 Serum/plasma cytokine tests Increased levels of IP-10 Adults Africa [86, 87]
 Antigen-specific antibodies Elevated levels of anti-Ag85A-binding IgG Infants Africa [63]
 Responses to latency antigens IFN-γ response to in vitro stimulation of PBMCs using HBHA Adults Europe [95]
IFN-γ response to in vitro stimulation of whole blood using Rv2628 Adults Europe [103]
 CD8+ T-cell response IFN-γ response to in vitro RD1 stimulation of PBMCs Children and adults Africa Europe [37]

Acronyms: LTBI: latent TB infection; RD: region of difference; IGRA: interferon (IFN)-γ release assays; PPD: purified protein derivative; TST: tuberculin skin test; HLA-DR: D-related human leukocyte antigen; IL: interleukin; AIRE: autoimmune regulator; BCG: bacille Calmette–Guérin; Ag: antigen; Th: T-helper cell; IP: IFN-γ-inducible protein; Ig: immunoglobulin; PBMCs: peripheral blood mononuclear cells; HBHA: heparin-binding haemagglutinin. 

Conclusion: Further studies are needed to determine whether correlates of risk can be used to prevent active TB through targeted prophylactic treatment, or to allow targeted enrolment into efficacy trials of new TB vaccines and therapeutic drugs.

 

Citation: Petruccioli E, Scriba TJ, Petrone L, Hatherill M, Cirillo DM, Joosten SA, Ottenhoff TH, Denkinger CM, Goletti D. Correlates of tuberculosis risk: predictive biomarkers for progression to active tuberculosis. European Respiratory Journal, 48(6):1751-1763. Click here.